Browsing by Author Mateus, Joana
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| Issue Date | Title | Author(s) | Type | Access Type |
| Mar-2024 | Cholesterol redistribution triggered by CYP46A1 gene therapy improves major hallmarks of Niemann-Pick type C disease but is not sufficient to halt neurodegeneration | Nunes, Maria João; Carvalho, Andreia Neves; Reis, Joana; Costa, Daniela; Moutinho, Miguel; Mateus, Joana; Mendes de Almeida, Rita; Brito, Sara; Risso, Daniela; Nunes, Sofia; Castro-Caldas, Margarida; Gama, Maria João; Rodrigues, Cecília M. P.; Xapelli, Sara; Diógenes, Maria José; Cartier, Nathalie; Chali, Farah; Piguet, Françoise; Rodrigues, Elsa | article |  |